Completed

Trial of Systemic Neoadjuvant Chemotherapy for Group B Intraocular Retinoblastoma

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What is being tested

Carboplatin

+ Cryosurgery

+ Infrared Laser Therapy

DrugProcedureRadiation
Who is being recruted

Until 5 Years
See all eligibility criteria
How is the trial designed

Treatment Study

Phase 3
Interventional
Study Start: December 2005
See protocol details

Summary

Principal SponsorChildren's Oncology Group
Last updated: January 28, 2026
Sourced from a government-validated database.Claim as a partner

Study start date: December 26, 2005

Actual date on which the first participant was enrolled.

PRIMARY OBJECTIVES: I. Determine the 2-year event-free survival of patients with Group B intraocular retinoblastoma treated with neoadjuvant chemoreduction comprising carboplatin and vincristine and standardized local ophthalmic therapy. SECONDARY OBJECTIVES: I. Determine the response rate after one course of chemoreduction (before standardized local ophthalmic therapy) in these patients. II. Correlate response rate with event-free survival in patients treated with this regimen. III. Determine the incidence of toxic effects in patients treated with this regimen. OUTLINE: This is a multicenter study. Patients receive chemoreduction comprising carboplatin IV over 60 minutes followed by vincristine IV over 1-2 minutes on day 1. Treatment repeats every 28 days for 6 courses in the absence of disease progression or unacceptable toxicity. After the first course of chemoreduction, patients undergo standardized local ophthalmic therapy comprising local laser therapy, cryotherapy, and/or radioactive plaque comprising iodine I 125 or ruthenium Ru 106. Patients are followed every 3-4 weeks until there is no active tumor seen on a minimum of 3 ophthalmic exams under anesthesia, every 6-8 weeks until 3 years of age, every 4-6 months until 10 years of age, and then annually thereafter.

Official TitleTrial of Systemic Neoadjuvant Chemotherapy for Group B Intraocular Retinoblastoma
NCT00079417
Principal SponsorChildren's Oncology Group
Last updated: January 28, 2026
Sourced from a government-validated database.Claim as a partner

Protocol

This section provides details of the study plan, including how the study is designed and what the study is measuring.
Design Details

28 patients to be enrolled

Total number of participants that the clinical trial aims to recruit.

Treatment Study

These studies test new ways to treat a disease, condition, or health issue. The goal is to see if a new drug, therapy, or approach works better or has fewer side effects than existing options.



Eligibility

Researchers look for people who fit a certain description, called eligibility criteria: person's general health condition or prior treatments.
Criteria

Any sex

Biological sex of participants that are eligible to enroll.

Until 5 Years

Range of ages for which participants are eligible to join.

Healthy volunteers not allowed

If individuals who are healthy and do not have the condition being studied can participate.

Criteria

Inclusion Criteria: * Newly diagnosed Group B intraocular retinoblastoma meeting 1 of the following criteria: * Group B tumor(s) in 1 eye * Group B tumor(s) in both eyes * Group A tumor in 1 eye and Group B tumor(s) in the other eye * Group E tumor in 1 eye that has been enucleated and Group B tumor(s) in the remaining eye at the time of enucleation of the Group E tumor * Defined by the International Classification System for Intraocular Retinoblastoma as follows: * Group A: Small tumors (≤ 3 mm in greatest dimension) confined to the retina, away from foveola and disc meeting the following criteria: * More than 3 mm from fovea * More than 1.5 mm from optic disk * Group B: Tumors more than 3 mm meeting the following criteria: * Confined to the retina in any location not in Group A * Tumor associated subretinal fluid \< 3 mm from the tumor margin with no subretinal seeding * Group E: Must have ≥ 1 of the following present: * Tumor touching the lens * Tumor anterior to anterior vitreous face involving ciliary body or anterior segment * Diffuse infiltrating retinoblastoma * Neovascular glaucoma * Opaque media from hemorrhage * Tumor necrosis with aseptic orbital cellulites * Phthisis bulbi * Confirmation of diagnosis by CT scan or MRI of the brain and orbits AND an ophthalmologic evaluation under anesthesia within the past 3 weeks * No choroidal and/or optic nerve invasion past the lamina cribosa * No evidence of extraocular retinoblastoma clinically or by head and orbital MRI and/or CT scan * No tumor present on histological exam at the cut end of the optic nerve for any Group E eye enucleated before study entry * Performance status - ECOG 0-2 * Bilirubin ≤ 1.5 times upper limit of normal (ULN) for age * AST or ALT \< 2.5 times ULN for age * Creatinine clearance (based on Schwartz formula) or radioisotope glomerular filtration rate ≥ 70mL/min/1.73 m\^2 * No prior chemotherapy * No other concurrent chemotherapy * No prior radiotherapy * No other concurrent radiotherapy, including intensity-modulated stereotactic, or proton beam radiotherapy * Prior enucleation of one eye allowed provided the remaining eye is Group B * No concurrent enucleation * No prior local ophthalmic therapy for retinoblastoma * No other prior therapy for retinoblastoma * No local therapy during chemotherapy course 1

Study Plan

Find out more about all the medication administered in this study, their detailed description and what they involve.
Treatment Groups
Study Objectives

One single intervention group is designated in this study

This study does not include a placebo group 

Treatment Groups

Group I

Experimental
Patients receive chemoreduction comprising carboplatin IV over 60 minutes followed by vincristine IV over 1-2 minutes on day 1. Treatment repeats every 28 days for 6 courses in the absence of disease progression or unacceptable toxicity. After the first course of chemoreduction, patients undergo standardized local ophthalmic therapy comprising local laser therapy, cryotherapy, and/or radioactive plaque comprising iodine I 125 or ruthenium Ru 106.

Study Objectives

Primary Objectives

Secondary Objectives

Study Centers

These are the hospitals, clinics, or research facilities where the trial is being conducted. You can find the location closest to you and its status.

This study has 10 locations

Suspended

Children's Hospital Los Angeles

Los Angeles, United StatesOpen Children's Hospital Los Angeles in Google Maps
Suspended

Lurie Children's Hospital-Chicago

Chicago, United States
Suspended

Dana-Farber Cancer Institute

Boston, United States
Suspended

Wayne State University/Karmanos Cancer Institute

Detroit, United States
Completed10 Study Centers